FDA approved levacetylleucine (Aqneursa) for ataxia in ataxia-telangiectasia, the first therapy for the disease, in patients 15 kg or heavier.
|Slideshows|January 15, 2020
11 clinical tips for treating congenital limb deficiency
Treating a child with a congenital limb deficiency can be a challenge. It is imperative that the clinician care not only for the child, but the family, and cover not only physical health, but mental health and educational progress. Here are 11 tips to improve care in your practice.
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Updated AAP guidance changes iron deficiency screening and treatment in children
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FDA grants priority review to efzimfotase alfa for hypophosphatasia in patients aged 2 years and older
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FDA approves levacetylleucine as first treatment for ataxia in ataxia-telangiectasia
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Pegcetacoplan reduces proteinuria, stabilizes kidney function in adolescents with C3G and IC-MPGN
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