FDA approved levacetylleucine (Aqneursa) for ataxia in ataxia-telangiectasia, the first therapy for the disease, in patients 15 kg or heavier.
|Articles|December 1, 2012
Contemporary Pediatrician, Digital Edition, September 2012
Sickle Cell Disease : Advice for treating emergencies Cyclic vomiting syndrome : Clinical features and comorbidities Care of children with autism : In the ED and other medical settings Dermcase : What a bloody mess A Psuedo Puzzler : Baby girl with hip dysplasia
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