FDA approved levacetylleucine (Aqneursa) for ataxia in ataxia-telangiectasia, the first therapy for the disease, in patients 15 kg or heavier.
|Articles|January 1, 2005
PEDIATRIC PUZZLER: An unexpected turn in an adolescent's case of headache and vision loss
This 15-year-old girl does not appear to be in any acute distress, but her cautious gait reminds you of a person walking in the dark.
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