For Contemporary Pediatrics, Dr Bobby Lazzara discusses a multicenter observational study published in JAMA Neurology that looked at time to treatment in children with refractory convulsive status epilepticus and the impact on mortality.
For Contemporary Pediatrics, Dr Bobby Lazzara discusses a multicenter observational study published in JAMA Neurology that looked at time to treatment in children with refractory convulsive status epilepticus and the impact on mortality.
Treatment candidate for limp-girdle muscular dystrophy receives Rare Pediatric Designation
June 18th 2024The company also announced that it has surpassed its interim analysis enrollment target and expects topline phase 3 data from the FORTIFY study (NCT05775848) among individuals with LGMD21/R9 in 2025.