Roberto Fernández Galán, PhD, assistant professor, Department of Neurosciences, at Case Western Reserve University School of Medicine, Cleveland, Ohio, discusses his study on the "noisy brain" of children with autism with Karen Donley-Hayes.
Roberto Fernández Galán, PhD, assistant professor, Department of Neurosciences, at Case Western Reserve University School of Medicine, Cleveland, Ohio, discusses his study on the "noisy brain" of children with autism with Karen Donley-Hayes.
Cerliponase alfa FDA approved to slow loss of ambulation in children of all ages with CLN2 disease
July 25th 2024From baseline to final assessment, all 7 matched cerliponase alfa-treated children under 3 years of age maintained a motor score of 3, representing a "grossly normal gait, signifying a delay in disease onset," stated BioMarin.