FDA approved levacetylleucine (Aqneursa) for ataxia in ataxia-telangiectasia, the first therapy for the disease, in patients 15 kg or heavier.
|Articles|February 22, 2021
What's new on Contemporary Pediatrics: February 22 to February 26
A look at what to expect from Contemporary Pediatrics this week
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Donna Hallas, PhD, PPCNP-BC, CPNP, PMHS, FAANP, FAAN, discusses her frustration with the uptake in influenza vaccinations in recent years and what she hopes to see when the vaccine for coronavirus disease 2019 becomes authorized for use in a wider range of children.
The move to educating over Zoom has led to many questions about what it means children who required additional resources that aren’t available in the home. A new study looks at how the lack of exposure to language is affecting children with cochlear implants.
Plus, more of the latest news in pediatrics.
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Tallie Z. Baram, MD, talks about how adding a measure of childhood unpredictability to ACEs screening may help pediatricians identify children at risk for mental health problems.
Review some of the top stories from the Contemporary Pediatrics website over the last week, and catch up on anything you may have missed.
The FDA granted priority review to efzimfotase alfa for HPP in patients aged 2 years and older; a decision is expected in the first half of 2027.
Adolescent VALIANT subgroup data show pegcetacoplan cut proteinuria 75% vs placebo, supporting its expanded pediatric kidney indication.
The FDA approved Fayuvi (rebisufligene etisparvovec-hopf), a one-time AAV9 gene therapy, as the first treatment for pediatric MPS IIIA (Sanfilippo syndrome type A).
Aquestive resubmitted its NDA for dibutepinephrine sublingual film Anaphylm, citing new human factors and PK data addressing the FDA's CRL.
Melissa Wallach, MD, FAAP, discusses what pediatricians should know about updated screening, supplementation, and treatment recommendations for iron deficiency.
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Trending on Contemporary Pediatrics
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Updated AAP guidance changes iron deficiency screening and treatment in children
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FDA grants priority review to efzimfotase alfa for hypophosphatasia in patients aged 2 years and older
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FDA approves levacetylleucine as first treatment for ataxia in ataxia-telangiectasia
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Pegcetacoplan reduces proteinuria, stabilizes kidney function in adolescents with C3G and IC-MPGN
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