FDA approved levacetylleucine (Aqneursa) for ataxia in ataxia-telangiectasia, the first therapy for the disease, in patients 15 kg or heavier.
|Articles|May 24, 2021
What's new on Contemporary Pediatrics: May 24 to 28
A look at what to expect from Contemporary Pediatrics this week
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A report examines the trends in bronchiolitis hospitalizations and treatment usage over the past decade.
In cases of a child being abused, how often are the child’s siblings at risk of maltreatment. An investigation offers much-needed answers.
Plus, more great content from the Contemporary Pediatrics team.
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Tallie Z. Baram, MD, talks about how adding a measure of childhood unpredictability to ACEs screening may help pediatricians identify children at risk for mental health problems.
Review some of the top stories from the Contemporary Pediatrics website over the last week, and catch up on anything you may have missed.
The FDA granted priority review to efzimfotase alfa for HPP in patients aged 2 years and older; a decision is expected in the first half of 2027.
Adolescent VALIANT subgroup data show pegcetacoplan cut proteinuria 75% vs placebo, supporting its expanded pediatric kidney indication.
The FDA approved Fayuvi (rebisufligene etisparvovec-hopf), a one-time AAV9 gene therapy, as the first treatment for pediatric MPS IIIA (Sanfilippo syndrome type A).
Aquestive resubmitted its NDA for dibutepinephrine sublingual film Anaphylm, citing new human factors and PK data addressing the FDA's CRL.
Melissa Wallach, MD, FAAP, discusses what pediatricians should know about updated screening, supplementation, and treatment recommendations for iron deficiency.
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Trending on Contemporary Pediatrics
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Updated AAP guidance changes iron deficiency screening and treatment in children
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FDA approves levacetylleucine as first treatment for ataxia in ataxia-telangiectasia
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FDA grants priority review to efzimfotase alfa for hypophosphatasia in patients aged 2 years and older
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Teen sports supplements: What to recommend, use with caution, and avoid
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