The FDA approved Fayuvi (rebisufligene etisparvovec-hopf), a one-time AAV9 gene therapy, as the first treatment for pediatric MPS IIIA (Sanfilippo syndrome type A).
|Articles|August 12, 2020
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As a professional organization in its fifth decade, NAPNAP is rich in experience and history when it comes to advanced practice nursing and children’s healthcare.
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As a professional organization in its fifth decade, NAPNAP is rich in experience and history when it comes to advanced practice nursing and children’s healthcare. Based on the expertise of our advanced nursing leaders and members, we release
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