Amélie Lothe, PhD, discusses findings showing early, sustained benefits of fenfluramine treatment for patients with Lennox-Gastaut syndrome.
|Articles|May 1, 2007
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Intractable crying in infants and young children can be a language all of its own-capable of communicating underlying disease. Here's what pediatricians need to know to avoid getting lost in translation.
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FDA approved levacetylleucine (Aqneursa) for ataxia in ataxia-telangiectasia, the first therapy for the disease, in patients 15 kg or heavier.
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Review some of the top stories from the Contemporary Pediatrics website over the last week, and catch up on anything you may have missed.
The FDA granted priority review to efzimfotase alfa for HPP in patients aged 2 years and older; a decision is expected in the first half of 2027.
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Aquestive resubmitted its NDA for dibutepinephrine sublingual film Anaphylm, citing new human factors and PK data addressing the FDA's CRL.
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Updated AAP guidance changes iron deficiency screening and treatment in children
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FDA grants priority review to efzimfotase alfa for hypophosphatasia in patients aged 2 years and older
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FDA approves levacetylleucine as first treatment for ataxia in ataxia-telangiectasia
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Fenfluramine shows sustained seizure reduction, functional improvement in Lennox-Gastaut syndrome
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