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Ersodetug misses primary endpoint in phase 3 sunRIZE trial for congenital hyperinsulinism | Image Credit: © ThawKyar - stock.adobe.com.
May 4th 2026
Ersodetug misses primary endpoint in phase 3 sunRIZE trial for congenital hyperinsulinism

Phase 3 sunRIZE trial of ersodetug in congenital hyperinsulinism missed its primary endpoint but showed CGM-based glycemic gains.

FDA Approves First Gene Therapy for Genetic Hearing Loss | Credit: Adobe Stock
April 23rd 2026

FDA approves first gene therapy for genetic hearing loss

FDA approves Zycubo for treating Menkes disease in children
January 13th 2026

FDA approves Zycubo for treatment of Menkes disease in children

FDA approves fibrinogen, human-chmt for acute bleeding in congenital fibrinogen deficiency | Image credit: Contemporary Pediatrics
December 19th 2025

FDA approves fibrinogen, human-chmt for acute bleeding in congenital fibrinogen deficiency

Early genetic testing may reshape care for inherited connective tissue disorders in children | Image Credit: © vegefox.com - stock.adobe.com.
November 19th 2025

Early genetic testing may reshape care for inherited connective tissue disorders in children

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Is TNF-Like Ligand 1A (TL1A) Inhibition the Answer to Improving Disease Remission in Inflammatory Bowel Disease?
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Is TNF-Like Ligand 1A (TL1A) Inhibition the Answer to Improving Disease Remission in Inflammatory Bowel Disease?

Jordan Axelrad, MD, MPH, FACG, FCCF; Jessica R. Allegretti, MD, MPH; Florian Rieder, MD

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