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FDA grants RPDD to CSTI-500 for treating pediatric Prader-Willi Syndrome | Image Credit: © wladimir1804 - © wladimir1804 - stock.adobe.com.
FDA grants RPDD to CSTI-500 for treating pediatric Prader-Willi Syndrome

July 25th 2024

ConSynance Therapeutics' CSTI-500, an innovative Triple Monoamine Reuptake Inhibitor, has received FDA's Rare Pediatric Disease Designation for treating Prader-Willi Syndrome in children.

Mirdametinib NDA submitted to treat children, adults with NF1-PN | Image Credit: © Araki Illustrations - © JAraki Illustrations - stock.adobe.com.
Mirdametinib NDA submitted to treat children, adults with NF1-PN

July 2nd 2024

FDA approves pitolisant for narcolepsy patients aged 6 years and older | Image Credit: © Calin - © Calin - stock.adobe.com.
FDA approves pitolisant for narcolepsy patients aged 6 years and older

June 24th 2024

Treatment candidate for limp-girdle muscular dystrophy receives Rare Pediatric Designation | Image Credit: © Araki Illustrations - © Araki Illustrations - stock.adobe.com.
Treatment candidate for limp-girdle muscular dystrophy receives Rare Pediatric Designation

June 18th 2024

Image Credit: Contemporary Pediatrics
OnabotulinumtoxinA shows promise for treating chronic migraine

June 17th 2024

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